Introduction Executive Summary Facioscapulohumeral Muscular Dystrophy: Overview • Causes • Mechanism of Action • Signs and Symptoms • Diagnosis • Disease Management Pipeline Therapeutics • Comparative Analysis Therapeutic Assessment • Assessment by Product Type • Assessment by Stage and Product Type • Assessment by Route of Administration • Assessment by Stage and Route of Administration • Assessment by Molecule Type • Assessment by Stage and Molecule Type Mid Stage Products (Phase II) • Comparative Analysis Losmapimod: Fulcrum Therapeutics • Product Description • Research and Development • Product Development Activities Drug profiles in the detailed report….. Early Stage Products (Phase I/II) • Comparative Analysis ATYR1940: aTyr Pharma, Inc. • Product Description • Research and Development • Product Development Activities Drug profiles in the detailed report….. Preclinical stage products • Comparative Analysis ARO DUX4: Arrowhead Pharmaceuticals • Product Description • Research and Development • Product Development Activities Drug profiles in the detailed report….. Inactive Products • Comparative Analysis Facioscapulohumeral Muscular Dystrophy Key Companies Facioscapulohumeral Muscular Dystrophy Key Products Facioscapulohumeral Muscular Dystrophy- Unmet Needs Facioscapulohumeral Muscular Dystrophy- Market Drivers and Barriers Facioscapulohumeral Muscular Dystrophy- Future Perspectives and Conclusion Facioscapulohumeral Muscular Dystrophy Analyst Views Facioscapulohumeral Muscular Dystrophy Key Companies Appendix

Table 1 Total Products for Facioscapulohumeral Muscular Dystrophy Table 2 Late Stage Products Table 3 Mid Stage Products Table 4 Early Stage Products Table 5 Pre-clinical & Discovery Stage Products Table 6 Assessment by Product Type Table 7 Assessment by Stage and Product Type Table 8 Assessment by Route of Administration Table 9 Assessment by Stage and Route of Administration Table 10 Assessment by Molecule Type Table 11 Assessment by Stage and Molecule Type Table 12 Inactive Products

• aTyr Pharma, Inc. • Fulcrum Therapeutics • Avidity Biosciences • Arrowhead Pharmaceuticals • Dyne Therapeutics • Genea Biocells • Evotec SE/Facio Therapies • miRecule